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  1. ReGenX Biosciences developed a gene therapy for Hunter syndrome, and the FDA requested longer-term pivotal results.

ReGenX Biosciences submitted data to the FDA in response to a request for longer-term pivotal results for its gene therapy.

2 reports, 1 independent Updated Aug 19
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ReGenX Biosciences submitted data to the FDA in response to a request for longer-term pivotal results for its gene therapy.

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